News
FDA Approves Sickle Cell Gene Therapy for Young Kids
56+ min ago (292+ words) The FDA on Wednesday expanded the approvalopens in a new tab or window for exagamglogene autotemcel (exa-cel, Casgevy) in severe sickle cell disease with recurrent vaso-occlusive crises and transfusion-dependent beta thalassemia to include children 2 years and up. Exa-cel, the first…...
Governance Overhaul for Human Embryo Model Research
1+ hour, 58+ min ago (704+ words) Mirage News Human embryo models can help researchers study early human development and infertility without relying solely on human embryos. As the technology advances, these models are becoming more complex and can be maintained in culture for longer periods. These…...
US FDA approves Vertex's gene therapy for sickle cell disease in children as young as two
13+ hour, 46+ min ago (255+ words) July 1 (Reuters) " The U. S. Food and Drug Administration approved expanded use of Vertex Pharmaceuticals" gene therapy in children as young as "two with inherited blood disorders, including sickle "cell disease, the first such treatment cleared for this age group. Casgevy, a…...
Vertex gets paediatric FDA okay for Casgevy gene therapy
7+ hour, 58+ min ago (537+ words) For the first time, children in the US as young as two with the blood disorders sickle cell disease and beta thalassaemia are eligible for Vertex Pharma's one-shot gene therapy Casgevy. The FDA has approved use of CRISPR Therapeutics-partnered Casgevy…...
Rewriting genetic medicine
9+ hour, 5+ min ago (317+ words) Source: Supplied by Scribe Benjamin Oakes co-founded Scribe Therapeutics in 2017 "We're now essentially reforging these really interesting DNA-targeting technologies to something that looks a lot more like a therapeutic,' says Benjamin Oakes, chief executive of Scribe Therapeutics " a US-based genetic…...
Cartherics emerges as Asia Pacific leader in off-the-shelf immune cell therapy
17+ hour, 1+ min ago (227+ words) Cartherics has been recognised as the Emerging Leader in Allogeneic Cell Therapy at the Asia Pacific Cell and Gene Therapy Excellence Awards 2026, a milestone that highlights the company's rise in the off-the-shelf immune cell therapy field. Based in Melbourne, the…...
HIV Can Convert T Cells From Helpers to Killers
19+ hour, 23+ min ago (210+ words) Some CD4 T cells infected with HIV can take on the characteristics of CD8 cells, according to a study published in Science. The researchers found that this transformed population of induced CD8 cells can still harbor latent HIV and contributes to the viral…...
CAR T Cells Simultaneously Target Glioblastoma and Immune Cells
23+ hour, 21+ min ago (517+ words) Inside Precision Medicine Scientists have identified a new molecular target for CAR T-cell immunotherapy to attack both glioblastoma cells and tumor-supporting macrophages at once. A study published today in Nature shows promising preclinical results that could allow this approach to…...
California start-up claims it can turn stem cells into human egg cells
1+ day, 2+ hour ago (286+ words) New Delhi: Conception, a California-based biotechnology start-up claims that it has found a way to turn stem cells into human egg cells. It shared its update on X on Wednesday calling the breakthrough a "big deal" which had the potential…...
A discarded Amgen T cell engager comes back to life at its California creator, 92 Bio
1+ day, 3+ hour ago (71+ words) Endpoints News A dis'card'ed Am'gen T cell en'gager comes back to life at its Cal'i'for'nia cre'ator, 92 Bio A small Cal'i'for'nia start'up is re'viv'ing an ex'per'i'men'tal T cell en'gager that its sci'en'tists orig'i'nal'ly de'vel'oped but had hand'ed off to Am'gen years…...