Please confirm you are human
This browser or connection looks automated. Press and continuously hold the control for 3 seconds to enable Google-hosted web results and, when separately allowed, AI-assisted answers.
A successful check enables 100 search requests. Interactive access does not authorize scraping, systematic collection, or reuse of search output.
News
What Goes Into Restarting A Shelved Orphan Drug Candidate?
19+ min ago (1109+ words) Guest Column | August 19, 2026 A conversation between Elizabeth White of the Orphan Therapeutics Accelerator and Life Science Connect's Jon O'Connell No advanced therapy developer feels good about abandoning a clinical-phase orphan drug candidate that they know has a real chance at…...
Andelyn Biosciences partners Queenâs University on AAV9-GM2 gene therapy manufacturing
2+ hour, 24+ min ago (294+ words) August 19, 2026 | Wednesday | News GM2 gangliosidoses are rare inherited lysosomal storage disorders caused by genetic mutations that disrupt normal lysosomal function. The resulting accumulation of harmful substances in cells leads to progressive damage to nerve cells in the brain and spinal cord....
UC San Diego Joins IGI to Build Next-Gen Genome Editing Tools
4+ hour, 43+ min ago (1005+ words) The Innovative Genomics Institute was founded in 2015 by Jennifer Doudna and Emmanuelle Charpentier’s CRISPR discovery to translate gene editing into practical solutions for society. It began as a partnership between UC Berkeley and UC San Francisco focused on human health,…...
Hong Kong???s First PIC/S GMP-Certified Stem Cell Production Facility Established at Science Park
7+ hour, 3+ min ago (273+ words) Hong Kong's First PIC/S GMP Stem Cell Production Facility Bridges a Critical Gap from Research to Clinical Application Patients, Families and Doctors Share First-hand Stories of the Journey from Cell Banking to Clinical Breakthroughs The event also featured first-hand…...
Scientists make breakthrough in replacing laboratory animals with human 'organ sacks"
8+ hour, 43+ min ago (763+ words) Legendary drummer dies aged 77 just weeks after pulling out of band's tour WATCH NOW: Hepatologist Dr Samia Ajaz discusses new scientific methods to reverse ageing The discovery could help save endangered species Scientists have made a breakthrough that may make…...
Embedding Regulatory Strategy in Cell and Gene Therapy Development
6+ hour, 29+ min ago (608+ words) Genetic Engineering and Biotechnology News Credit: DrAfter123 / Getty Images Jeffrey Mocny, PhD, VP Scientific Leadership for Rose BioSolutions translates client needs into actionable development and manufacturing programs that help clients achieve their therapeutic development goals. Mocny leads a team of scientists…...
Tackling rare genetic disorders with patient-focused science
12+ hour, 53+ min ago (643+ words) by Stefanie Koperniak | Office of Graduate Education | August 18, 2026August 18, 2026 Shannon Knight, a brain and cognitive sciences PhD candidate and McGovern Institute researcher, focuses on developing a novel gene therapy. Shannon Knight attributes her interest in neuroscience to an experience she had…...
Gene Editing Used To Create Hypoallergenic Beagles
13+ hour, 59+ min ago (94+ words) Smoggy with a soupcon of ragweed Geneticists used CRISPR to produce twin beagle pups who do not make the lead allergy-causing protein found in dogs, opening up new possibilities for gene-editing technologies. What do you think? “One day I’ll be…...
Meet the world’s first CRISPR-edited hypoallergenic hounds
15+ hour, 5+ min ago (20+ words) Using CRISPR, researchers have created a pair of hypoallergenic dogs that don’t produce the main protein that triggers dog allergies....
Red Blood Cell-Inspired Carriers Show Promise for Gene Therapy Delivery
15+ hour, 6+ min ago (724+ words) Red blood cells serve as the foundation for nanocarriers that show promise in a new study as effective and efficient vehicles for gene therapy, tumor targeting and other medical treatments. Scientists at The Ohio State University showed that the engineered…...